CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect

PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs

PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs

PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs

CRISPR/Cas9-based targeting of fluorescent reporters to human iPSCs to isolate atrial and ventricular-specific cardiomyocytes

PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs

Functional genomics and the future of iPSCs in disease modeling - ScienceDirect

Oxidative stress monitoring in iPSC-derived motor neurons using genetically encoded biosensors of H2O2

Cold shock' increases the frequency of homology directed repair gene editing in induced pluripotent stem cells

Correction of the DYSF Gene in Miyoshi Myopathy

Optic nerve regeneration screen identifies multiple genes restricting adult neural repair - ScienceDirect

Gene regulation analysis of patient-derived iPSCs and its CRISPR-corrected control provides a new tool for studying perturbations of ELMOD3 c.512A>G mutation during the development of inherited hearing loss

Nanoparticles-mediated CRISPR-Cas9 gene therapy in inherited retinal diseases: applications, challenges, and emerging opportunities, Journal of Nanobiotechnology

Dominant optic atrophy, OPA1, and mitochondrial quality control: understanding mitochondrial network dynamics, Molecular Neurodegeneration

Molecular Therapy - Methods & Clinical Development, Gene Editing