TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.

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TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

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TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease