The pathogenesis of Niemann–Pick type C disease: a role for autophagy?, Expert Reviews in Molecular Medicine

Parents of kids with Niemann Pick C advocate for adrabetadex

Niemann-Pick Type C « Niemann-Pick Children's Fund, Inc

IJMS, Free Full-Text

National Niemann-Pick Disease Foundation, Inc. - October is Global Niemann- Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to the NNPDF go to www.nnpdf.org. #niemannpick #ASMD #

Niemann-Pick Type C Disease - NP-C Genetic Disease - Lysosomal Disease

Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library

Revista de Pediatria SOPERJ

Niemann-Pick type C disease is associated with mtDNA disorganization.

Main therapies and point of action in Niemann type C disease.

Impaired Autophagy in the Lipid-Storage Disorder Niemann-Pick Type C1 Disease - ScienceDirect